OnCo
targetsTarget

HER2

A growth-signal receptor. Some cancers make far too much of it, and drugs that block it or use it as a docking site have transformed those cancers.

Human epidermal growth factor receptor 2 is a receptor tyrosine kinase amplified in ~15-20% of breast cancers and a subset of gastric, colorectal, lung (mutations), and biliary cancers. Trastuzumab (1998) was the first targeted antibody in solid tumours. Trastuzumab deruxtecan redefined the target by working in 'HER2-low' tumours that older drugs ignored, and in 2026 gained approval in early-stage disease.

HER2: what it is and how drugs act on it · animated schematic, not to scale
  • Target · the protein and the cell it sits on
  • Drug · antibody, small molecule, cell or radioligand
  • Effect · signal, damage or kill

In plain words · A growth-signal receptor. Some cancers make far too much of it, and drugs that block it or use it as a docking site have transformed those cancers.

  1. 1 · What it is

    A growth-signal receptor. Some cancers make far too much of it, and drugs that block it or use it as a docking site have transformed those cancers.

  2. 2 · What goes wrong in cancer

    Ligand-less receptor that heterodimerises with HER3/EGFR to drive PI3K and MAPK signalling. Amplification is a true oncogenic driver; low expression is merely a delivery address for ADCs.

  3. 3 · How drugs use it

    20 products aim at HER2: antibodies, antibody-drug conjugates, bispecific antibodies and small molecules. Because it sits on the outside of the cell, it can be reached from the bloodstream: antibodies flag the cell, ADCs deliver a toxin, radioligands deliver radiation, and CAR-T or bispecifics bring a T cell.

Biology

Ligand-less receptor that heterodimerises with HER3/EGFR to drive PI3K and MAPK signalling. Amplification is a true oncogenic driver; low expression is merely a delivery address for ADCs.

Where it is found
  • HER2+ breast cancer (~15-20%)
  • HER2-low breast cancer (~50%)
  • Gastric/GEJ (~15-20%)
  • HER2-mutant NSCLC (~2-3%)
  • Colorectal (~3-5%)
  • Biliary tract
Class
surface antigen · ERBB2

How common it is, by cancer

CancerPrevalenceSource
HER2-positive breast cancer
100%
Nature
HR-positive / HER2-negative breast cancer
55-65%
Nature
Triple-negative breast cancer
30-40%
Nature
Gastric & gastro-oesophageal junction cancer
15-20%
Wikipedia
Biliary tract cancer
10-20%
Wikipedia
Colorectal cancer
3-5%
Wikipedia
Non-small-cell lung cancer
2-3%
cBioPortal (TCGA)

Approximate, population-level figures; the measure column says what was counted. Ranges show the midpoint as a bar.

Products

20top
Not mapped hereSmall-molecule pan-ErbB TKI (second generation, irreversible)
Afatinib · Gilotrif / Giotrif

Afatinib (Gilotrif) is an irreversible EGFR pill for lung cancer, notable for activity against uncommon EGFR mutations (G719X, L861Q, S768I).

Phase 3ADC
ARX788

ARX788 is a HER2 ADC with a precisely placed, non-cleavable payload that beat lapatinib-capecitabine in China and showed activity in brain metastases.

Not filedADC
Disitamab vedotin

Disitamab vedotin is a Chinese HER2 ADC approved for gastric and bladder cancer, now in global trials with Pfizer.

ApprovedSmall-molecule reversible HER2/EGFR kinase inhibitor
Lapatinib · Tykerb

Lapatinib was the first HER2-blocking pill (2007) and is now mostly a comparator arm and a late-line option, displaced by tucatinib and ADCs.

ApprovedFc-engineered monoclonal antibody (anti-HER2)
Margetuximab · Margenza

A trastuzumab look-alike with an engineered tail that binds immune cells more tightly; approved in 2020 but rarely used after ADCs arrived.

ApprovedSmall-molecule irreversible pan-HER kinase inhibitor
Neratinib · Nerlynx

A pill taken for a year after trastuzumab to further reduce recurrence in HER2-positive, hormone-positive breast cancer, limited by severe diarrhoea.

ApprovedMonoclonal antibody (anti-HER2, dimerisation domain)
Pertuzumab · Perjeta; Phesgo (with trastuzumab, subcutaneous)

A second HER2 antibody that binds a different spot from trastuzumab, blocking HER2 from pairing with HER3; together they extended survival by 16 months in CLEOPATRA.

Not filedSmall-molecule irreversible pan-HER kinase inhibitor
Pyrotinib · Airuini

Pyrotinib is China's HER2 pill, widely used there with capecitabine and as a comparator for the new Chinese HER2 ADCs.

ApprovedSmall-molecule kinase inhibitor (HER2)
Sevabertinib · Hyrnuo

Sevabertinib is an oral HER2 inhibitor for lung cancers with HER2 mutations, approved in November 2025 as an alternative to Enhertu and zongertinib.

ApprovedMonoclonal antibody (anti-HER2)
Trastuzumab · Herceptin (and biosimilars, Phesgo with pertuzumab)

The first targeted antibody for a solid tumour (1998), which turned HER2-positive breast cancer from the worst subtype into one of the most treatable.

ApprovedBiosimilar monoclonal antibody (anti-HER2)
Trastuzumab biosimilars · Ogivri, Herzuma, Kanjinti, Trazimera, Ontruzant, Hercessi

Near-identical copies of Herceptin, approved since 2017, that cut the price of HER2 treatment and widened access worldwide.

Phase 3ADC
Trastuzumab brengitecan

SystImmune's HER2 ADC, sharing its payload with iza-bren, now in a 1,450-patient trial to replace Kadcyla after surgery.

ApprovedADC
Trastuzumab deruxtecan · Enhertu

Trastuzumab deruxtecan (Enhertu) is the most successful ADC ever. It redefined HER2 by working in tumours with only tiny amounts of the protein, and in 2026 moved into early-stage breast cancer.

WithdrawnADC
Trastuzumab duocarmazine

A HER2 ADC with a DNA-alkylating payload that beat chemotherapy in a phase 3 trial yet never reached the market, because eye and lung toxicity and a stronger rival arrived first.

ApprovedADC
Trastuzumab emtansine · Kadcyla

Trastuzumab emtansine (Kadcyla, T-DM1) was the first ADC for a solid tumour (2013). It is still standard after surgery for HER2+ breast cancer patients whose tumour did not fully respond to pre-surgery treatment.

Not mapped hereADC
Trastuzumab rezetecan

Hengrui's HER2 ADC, approved in China for lung cancer and showing Enhertu-scale results in breast cancer, part of a wave of Chinese ADCs heading for global trials.

ApprovedSmall-molecule kinase inhibitor (HER2)
Tucatinib · Tukysa

A HER2-selective pill that works in the brain, for HER2-positive breast cancer with brain metastases.

ApprovedBiparatopic bispecific antibody (HER2)
Zanidatamab · Ziihera

Zanidatamab (Ziihera) is an antibody that grabs HER2 at two different spots, approved for HER2+ bile duct cancer.

ApprovedBispecific antibody (HER2×HER3)
Zenocutuzumab · Bizengri

Zenocutuzumab is the first drug for cancers driven by NRG1 gene fusions, working by blocking HER3 from receiving its growth signal.

ApprovedSmall-molecule kinase inhibitor (HER2)
Zongertinib · Hernexeos

Zongertinib was the first oral HER2 inhibitor for lung cancer with HER2 mutations, approved in 2025 and moved to first line in 2026.

Key papers

4top
rctNew England Journal of Medicine 2024changed practice
DESTINY-Breast06: trastuzumab deruxtecan before any chemotherapy in hormone-receptor-positive, HER2-low or ultralow breast cancer

Patients with hormone-receptor-positive metastatic breast cancer that has stopped responding to endocrine therapy can be offered trastuzumab deruxtecan as their first chemotherapy-type treatment if the tumour shows any HER2 staining, rather than waiting until after conventional chemotherapy. Whether to use it before or after chemotherapy is now a choice, since overall survival was not shown to differ and the drug carries a risk of lung inflammation.

rctNew England Journal of Medicine 2022changed practice
DESTINY-Breast03: trastuzumab deruxtecan beats T-DM1 as second-line treatment of HER2-positive metastatic breast cancer

For HER2-positive metastatic breast cancer that has progressed after trastuzumab and a taxane, trastuzumab deruxtecan is now the standard second-line treatment and T-DM1 has moved later in the sequence. The benefit is large enough that ADC design, not just the target, is understood to be what matters. Patients need lung monitoring because of the risk of pneumonitis.

rctNew England Journal of Medicine 2022changed practice
DESTINY-Breast04: trastuzumab deruxtecan works in HER2-low breast cancer, creating a new treatable group

Patients whose breast cancer was previously called HER2-negative may now be eligible for an effective HER2-directed drug if their tumour has even low-level HER2 staining, so pathology reports must now distinguish HER2-low (1+ or 2+/ISH-negative) from HER2-zero. This applies to metastatic disease after at least one line of chemotherapy; it does not mean these patients benefit from trastuzumab or other older HER2 drugs.

rctNew England Journal of Medicine 2019changed practice
KATHERINE: switching to T-DM1 when HER2-positive breast cancer survives pre-surgery treatment

HER2-positive breast cancer is now routinely treated before surgery so that the pathology result can guide what comes after: patients with no residual cancer continue trastuzumab (with or without pertuzumab), while those with residual disease switch to T-DM1. This model of using the tumour's response as a test has since been copied in triple-negative and other cancers.

Latest papers

top
Literature trend5,673 papers in the last 12 months+21% vs prior 12How this is computed
Latest papers · live from Europe PMC
Open in Europe PMC

Query for this target: (TITLE:"HER2" OR ABSTRACT:"HER2" OR TITLE:"ERBB2" OR ABSTRACT:"ERBB2") AND (cancer OR tumor OR tumour OR oncology OR carcinoma OR lymphoma OR leukemia OR leukaemia OR myeloma OR sarcoma OR melanoma OR glioma). Results are unfiltered search hits about HER2, not a curated reading list.

Connected

124top

Pages like this

not linked directly; found by shared links

cancers

14

technologies

5

drugs

20

companies

2

institutions

11

pathways

10

terms

12

trials

11

pairings

1

ideas

9

people

22

bottlenecks

3

key papers

4