OnCo
ideasIdea

A funded programme of organ-preservation trials to avoid radical surgery

For some cancers, drugs and radiotherapy can now cure without removing the organ, sparing patients a stoma, a lost voice or a removed bladder. A dedicated programme would run the trials to prove where this is safe.

A trials programme testing non-operative and organ-preserving strategies against standard radical surgery: watch-and-wait after total neoadjuvant therapy in rectal cancer, immunotherapy-only in mismatch-repair-deficient tumours (following the dostarlimab rectal cancer results), bladder preservation with chemoradiotherapy and immunotherapy, larynx preservation, breast surgery omission after exceptional response, and oesophageal active surveillance. These trials are hard to fund because they remove a procedure rather than add a drug, but their quality-of-life value is large. The programme would include patient-reported outcomes and survivorship endpoints as co-primary, and shared surveillance protocols.

Hypothesis
A dedicated programme completes at least five randomised or well-controlled organ-preservation trials within seven years, at least three of which establish non-inferior survival with substantially better patient-reported function, changing guidelines in those indications.
Rationale
The OPRA and dostarlimab rectal cancer studies, the bladder-preservation trimodality data and the larynx-preservation trials show the biology allows organ preservation in selected patients; the barrier is the trials, which no company will fund and which surgical culture has been slow to run.
What would test it
Launch three trials in the first two years with pre-registered non-inferiority margins and patient-reported co-primary endpoints; track accrual and publication.
Maturity
being tested at scale
Who has to act
research
Cost to try
Large (over $50M)
Years to first evidence
5
Bottlenecks it attacks

Connected

13top

Pages like this

not linked directly; found by shared links