OnCo
ideasIdea

Rescue the biological samples from failed trials for biomarker research

Trials that fail still collected thousands of blood and tissue samples. Instead of being destroyed, they should be pooled so scientists can learn who might have benefited.

Negative trials are often the most informative for biomarker discovery: a subgroup may have responded. Samples from discontinued programmes are usually destroyed or locked. A biobank with pre-negotiated transfer terms, linked de-identified clinical data, and an access committee would allow prospective-retrospective biomarker studies and could resurrect drugs for a biomarker-defined population.

Hypothesis
At least two drugs from failed trials in the biobank will produce a validated predictive biomarker leading to a new enrichment trial within five years.
Rationale
Cetuximab in KRAS wild-type colorectal cancer and gefitinib in EGFR-mutant lung cancer were rescued retrospectively from broadly negative or marginal populations. Systematising sample rescue would make such rescues routine.
What would test it
Secure samples from five recently failed phase 3 oncology trials; fund two biomarker discovery studies; report time to access and findings.
Maturity
early clinical
Who has to act
research
Cost to try
Medium ($1M to $50M)
Years to first evidence
3
Bottlenecks it attacks

Connected

5top