OnCo
trialsTrialPositive

THOR

The first targeted pill to lengthen survival in bladder cancer, for the fifth of tumours with FGFR alterations.

Cohort 1: OS 12.1 vs 7.8 months (HR 0.64); PFS 5.6 vs 2.7. Cohort 2 (vs pembrolizumab in IO-naive patients) showed no benefit, so erdafitinib is positioned after immunotherapy. Full FDA approval January 2024. THOR-2 explored intravesical/oral use in NMIBC.

Setting
Advanced urothelial cancer with FGFR3/2 alterations after chemotherapy and a checkpoint inhibitor: erdafitinib vs chemotherapy (cohort 1)
Phase
Phase 3
Sponsor
Johnson & Johnson
Registry
Headline result
OS 12.1 vs 7.8 months, HR 0.64 (cohort 1).
Reported
2023
Enrolled
266
Replication
Cohort 2 (vs pembrolizumab) negative; benefit confined to the post-IO setting.

Outcomes

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In plain words
What these results mean for people, not percentages
266 people took part
Overall survival (cohort 1)primarysurvival endpoint
  • Median 12.1 vs 7.8 months with Erdafitinib compared with Chemotherapy; about 4.3 months longer for half the group.
  • A median is a midpoint: half the people did better than this and half did worse, so it is not a prediction for any one person.
  • Put another way, the treated group had about 36 percent lower chance of the event at any given time (hazard ratio 0.64, likely range 0.47 to 0.88).
  • Overall survival counts deaths from any cause, so it is the most direct measure of whether a treatment helps people live longer.
  • These results apply to the people the trial enrolled: Advanced urothelial cancer with FGFR3/2 alterations after chemotherapy and a checkpoint inhibitor: erdafitinib vs chemotherapy (cohort 1). People in a different situation may not see the same effect.
  • The trial selected people by a biomarker (FGFR3); the result should not be assumed for people whose cancer does not have it.

Numbers are from the trial as recorded here; see the source links in the table below. This is orientation, not medical advice: ask your team how closely the trial population matches you.

266 participants enrolled.

Overall survival (cohort 1)primary
HR 0.64 (0.47–0.88) · p = 0.005
Erdafitinib
12.1 mo
Chemotherapy
7.8 mo
Source
EndpointArmnValueHR (95% CI)pSource
Overall survival (cohort 1)primaryErdafitinib13612.1 months0.64 (0.47–0.88)0.005link
Chemotherapy1307.8 months
Replication
Cohort 2 (vs pembrolizumab) negative; benefit confined to the post-IO setting.

Connected

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