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RAMP 201

RAMP 201 produced the first approved treatment designed for low-grade serous ovarian cancer, a slow-growing type driven by the RAS pathway that shrugs off chemotherapy.

In KRAS-mutant tumours, the confirmed response rate was 44% with median PFS 19.6 months and median duration of response 31.1 months; response was lower in KRAS-wild-type disease (Targeted Oncology, 2025). FDA accelerated approval 8 May 2025 for KRAS-mutated recurrent LGSOC after prior systemic therapy. The confirmatory RAMP 301 phase 3 versus chemotherapy or endocrine therapy is ongoing.

Setting
Recurrent low-grade serous ovarian cancer: avutometinib (RAF/MEK clamp) + defactinib (FAK inhibitor)
Phase
Phase 2
Sponsor
Verastem
Registry
Headline result
ORR 44%, median PFS 19.6 months in KRAS-mutant LGSOC.
Reported
2024

Outcomes

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In plain words
What these results mean for people, not percentages
Objective response rate (KRAS-mutant)primaryresponse endpoint
  • 44 out of 100 people had their tumour shrink with Avutometinib + defactinib.
  • There was no comparison group, so this number cannot tell you how much of the effect is due to the treatment.
  • A response rate counts how many people had their tumours shrink by a set amount; shrinking is encouraging but does not by itself show that people live longer or feel better.
Progression-free survival (KRAS-mutant)surrogate endpoint
  • Median 19.6 months with Avutometinib + defactinib.
  • A median is a midpoint: half the people did better than this and half did worse.
  • This is a surrogate endpoint: it measures the cancer being controlled or absent on scans and tests, which often, but not always, translates into living longer.
Be careful
  • These results apply to the people the trial enrolled: Recurrent low-grade serous ovarian cancer: avutometinib (RAF/MEK clamp) + defactinib (FAK inhibitor). People in a different situation may not see the same effect.

Numbers are from the trial as recorded here; see the source links in the table below. This is orientation, not medical advice: ask your team how closely the trial population matches you.

Objective response rate (KRAS-mutant)primary
Avutometinib + defactinib44 of 100
Source
Progression-free survival (KRAS-mutant)
Avutometinib + defactinib
19.6 mo
Source
EndpointArmnValueHR (95% CI)pSource
Objective response rate (KRAS-mutant)primaryAvutometinib + defactinib44%link
Progression-free survival (KRAS-mutant)Avutometinib + defactinib19.6 monthslink

Connected

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