OnCo
pathwaysPathway

The p53 network (guardian of the genome)

p53 is the cell's emergency coordinator. Damage, oncogene stress, or lack of oxygen switch it on; it then pauses division, orders repairs, or triggers suicide or permanent retirement. MDM2 keeps it switched off in healthy cells. Half of all cancers break p53 outright; many of the rest over-produce MDM2.

Stress inputs converge on p53 stabilisation: DNA damage via ATM/ATR-CHK2/CHK1 phosphorylation, oncogene activation via p14ARF (CDKN2A) sequestering MDM2, ribosomal stress via RPL5/RPL11, hypoxia. MDM2 (with MDMX/MDM4) ubiquitinates p53 for proteasomal degradation and is itself a p53 target, forming a negative feedback loop. Active p53 tetramers transactivate CDKN1A (p21, arrest), PUMA/NOXA/BAX (apoptosis), GADD45/DDB2 (repair), TIGAR/SCO2 (metabolism), and senescence programmes; outcome depends on stress intensity and cofactors. TP53 mutations (~50% of cancers) are mostly missense DNA-binding-domain hotspots (R175, R248, R273) with dominant-negative and gain-of-function effects; MDM2 amplification (sarcoma, glioma) and MDM4 amplification (melanoma, retinoblastoma) silence wild-type p53. Drugs: MDM2 inhibitors (milademetan, brigimadlin, navtemadlin) in TP53-wild-type disease, limited by thrombocytopenia; Y220C reactivator rezatapopt; eprenetapopt (APR-246) failed in MDS; TP53 status guides WEE1/ATR synthetic lethality and predicts chemoresistance in CLL (del17p).

In one picture

A fire marshal who is normally kept locked in a cupboard (by MDM2). When alarms sound, the cupboard opens and the marshal stops work, calls repairs, and if the building is beyond saving, orders evacuation (apoptosis) or condemns it (senescence). Cancers either sack the marshal (TP53 mutation) or weld the cupboard shut (MDM2 amplification).

Diagram

top
Light up a product:
DNA damage (ATM/ATR)Oncogene stress → ARFHypoxia, ribosome stressMDM2 / MDMXp53TP53 mutation (~50%)p21 → arrestPUMA, NOXA → apoptosisSenescence, repairactivatesinhibitsdruggable target (click)hit by selected productescape route

How drugs attack it

4top
  • MDM2 inhibitors (brigimadlin, milademetan, navtemadlin) for TP53-wild-type, MDM2-amplified tumours
  • Mutant p53 reactivators: rezatapopt (Y220C); eprenetapopt failed in phase 3 MDS
  • TP53-mutant tumours are approached via WEE1, ATR, PLK1 dependence and via p53-independent chemotherapy
  • TP53 status as biomarker: del17p CLL, MDS/AML risk, Li-Fraumeni surveillance

Connected

25top

Pages like this

not linked directly; found by shared links