OnCo
ideasIdea

A mandatory over-70s cohort with geriatric assessment in every pivotal trial

Most people with cancer are over 65, but trials mostly enrol younger, fitter people. Requiring a group of older patients, assessed for frailty, in every big trial would show whether the drug works and is safe for those most likely to receive it.

Registrational trials include a pre-specified cohort or stratum of patients aged 70 and over, enrolled in proportion to disease incidence, with baseline geriatric assessment (function, cognition, comorbidity, falls, nutrition) recorded, and with efficacy, toxicity and dose modification reported by frailty category. FDA's Project Silver and the older-adults guidance support inclusion; the proposal makes it a quantitative requirement.

Hypothesis
Trials with an older-adult cohort will find clinically relevant differences in toxicity or dosing in a meaningful fraction of agents, leading to label guidance for frail patients at approval rather than years later.
Rationale
Older patients have different pharmacokinetics, more comorbidity and different goals; post-approval real-world toxicity is often higher than trial data predicted. Geriatric-assessment-guided care reduced toxicity in randomised trials.
What would test it
Compare the frequency of age- or frailty-specific label statements at approval for drugs with and without a mandated cohort, and real-world discontinuation rates in older patients.
Maturity
early clinical
Who has to act
regulator
Cost to try
Medium ($1M to $50M)
Years to first evidence
3
Bottlenecks it attacks

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